The Hermansky-Pudlak Syndrome Network is joining with a coalition of patient advocacy groups and groups representing medical researchers to support the creation of the National Center for Advancing Transitional Sciences (NCATS), a new center within the National Institutes of Health (NIH).
The purpose of NCATS will be to look for innovative ways to move high-need medical cures through the development pipeline faster. The new center will focus on research to re-engineer the traditional transitional process at the NIH and in the private sector to find ways to make the process more efficient. The goal is to help potential cures reach patients faster. It will not replace transitional research at the NIH or in the private sector. Areas of particular interest will include: target validation, biomarkers, pre-clinical toxicology, clinical trial design and effective adherence.