Skip to main content

Moving the cure forward

The fall and Christmas season are our biggest fundraising times of year. That is true for a lot of non-profits. Maybe people are in the giving spirit. Maybe they are thinking about tax deductions at the end of the year. Whatever it is, thank God for the donors, and thank God for the HPSers and supporters that help us with fundraisers! There will be no cure without all of you!

The HPS Network is growing and evolving. The opportunities for us out there to get closer to treatments, and a cure, are so many that we can’t even take advantage of them all. But, our budget has to keep up.

Soon we will be facing some hard choices. We are at a point that we need a full time nurse who is able to work on center recruitment and families who need help. Donna just can’t do it all. All of our part-time staff works for way, way, way under market value for their talents and positions. We are so lucky to have people so vested in our cause, and for whom making a difference is so important, that they are willing (or able) to work for so little. Still, we can’t keep moving forward as an organization relying on people able to work for peanuts. We need to pay enough that someone could actually pay their basic bills and work for us.

Right now, looking at our budget, the only way I see us able to do this is if we do not fund another American Thoracic Society grant. That is sooooo sad! These grants have done so much to move the research. They have had a tremendous return on investment!

Consider that the first junior researcher we funded with $30,000 a year for two years was Dr. Lisa Young. She turned her initial research that we helped fund (matched by the American Thoracic Society) into a $770,000 grant, and then a $2 million NIH grant. She is now leading the project to open the HPS research centers. Talk about a bargain!

The problem is we want to turn all of this research into clinical trials at some stage. We need to move it from the lab to trials and then to real treatments for real HPSers. If we don’t get some help in the office, we simply aren’t going to be able to do that. We won’t be able to take the investments made before now and turn them into real results for patients someday.

I blog about this only because in this fundraising season, I want us all to understand what choices we face. I want us all to understand how important fundraising is, and how we need everyone’s help! How much you raise isn’t important. It is a group effort.

If we don’t want to lose the research engine that the ATS grants have been, but still keep us moving forward toward another trial, then we need to increase our budget next year by at least $80,000.


The reality is HPS is rare. The people who care about curing it are the ones affected by it. It is up to us. It is on our hands. Please, help us keep moving forward to the cure!

Comments

Popular posts from this blog

Ratner's Cheesecake

Here's another recipe from Toby! Thanks Toby......and I'll get the others posted soon! Ratner's Cheesecake and plain cookies Ratner's was a Jewish dairy restaurant in the lower East Side of Manhattan. This recipe, from my disintegrating, no longer in print Ratner's cookbook, is the closest I've ever gotten to reproducing the rich, heavy cheesecake my mother made when I was a kid. It's worth the time it takes to prepare and every last calorie. Dough Can be prepared in advance. Makes enough for two cakes. Can be frozen or used to make cookies – see recipe below. 1 cup sugar 1 teaspoon vanilla extract 1 cup shortening 1 teaspoon lemon extract 1 cup butter 2 eggs 3 cups sifted cake flour ½ teaspoon salt 2 cups all purpose flour 1 teaspoon baking powder 1. In a bowl, combine all ingredients with hands. Refrigerate 3 -4 hours, or preferably overnight. Filling (for

The next generation with Hermansky-Pudlak Syndrome

I'm so behind on posting about the trip to Puerto Rico. Since the episode of Mystery Diagnosis on Hermansky-Pudlak Syndrome ran right after we got home, it's been a little busy. These, however, are my favorite pictures from Puerto Rico. I know, not pretty senery etc - but these little guys and gals inspire me. They are the next generation of folks with HPS, and if we keep up the hard work, they will live better lives because of it. They motivate me.

Some good news about Pirfenidone

Below is a press release from Intermune, the company that makes Pirfenidone. They have essentially reviewed the various clinical trials going on, and decided that Pirfenidone is safe and well tolerated. That would pretty much go along with what we've observed in the HPS community as well. We have a few folks that have been on the drug since the late 90s and continue to do well. Of course, as a journalist, I do have to say consider the source - but at the same time, as someone in a Pirfenidone trial, it's good to know. Results of Comprehensive Safety Analysis of pirfenidone In IPF Patients Presented At European Respiratory Meeting - Analysis shows safety and tolerability of pirfenidone across four clinical trials - VIENNA, Sept. 14 /PRNewswire-FirstCall/ -- InterMune, Inc. (Nasdaq: ITMN ) today announced that the results of a comprehensive review of safety data from four clinical studies were presented at the 2009 European Respiratory Society Annual Congress in Vienna, Austria