Skip to main content

In search of the perfect mouse

I’ve never been a big fan of mice. After a particularly traumatic experience with a Norwegian rat while living in Northern Germany, I’ve just had a kind of rodent phobia. Thus, it’s ironic that my future health is inextricably tied to colonies of little furry mice, passing their lives away in sterile little cages and tucked away in various labs across the world.

While at the American Thoracic Society meeting in San Diego, the lives, and thus benefits, of these little creatures were a major topic of consideration.

My very uneducated, and completely non-medical understanding of the debate is something like this. Scientists need mice to study potential therapies for pulmonary fibrosis, but as of yet, there seems to be no perfect mouse model. The thing about mice is they don’t live very long. Many genetic causes of pulmonary fibrosis develop over time, and mice that might have the genes to develop fibrosis typically die before it ever happens. Living in those nice little sterile cages, free from the toxins and intrusions of the world, probably doesn’t help either.

So, researchers studying treatments for pulmonary fibrosis have to find a way to speed up the fibrosis process. Right now the most accepted way to do this is to expose mice to bleomycin, a drug used to treat cancer that is known to cause pulmonary fibrosis a side effect.

The trouble is no one seems to be able to say for sure if when treating fibrosis in mice caused by bleomycin exposure, scientists are actually treating the underlying disease process, or simply repairing a lung injury.

Another alternative some scientists use is to expose mice to asbestos – which seems like even more of a problem to my uneducated mind, but what do I know?

Donna and I sat in several sessions as various mouse models were discussed. We scratched our heads. Why aren’t more scientists using the HPS mouse model? There’s no doubt that HPS mice (bred with two types of HPS) develop fibrosis – it’s a clear genetic cause – no guess work there about lung injury.

Why is the majority of the research community stuck on this bleomycin model? Sure, the HPS model has its faults too – but if none of the models are perfect, then why is the majority of research occurring with the bleomycin treated mice? Why don’t they at least mix it up a bit? Is it just that they don't know about HPS? Or, is there a better reason?

There are a few other reasons I think the HPS mouse model should get more consideration as an alternative mouse model – but I’ll comment more on those after Dr. Lisa Young publishes her research on this. She’s got some very interesting findings, and is already in a race to get them published.

If there’s some researcher out there who might stumble across this blog, and be able to explain it to me better, I’d appreciate some help understanding this; but it seems to me more use of the HPS mouse model would benefit research into idiopathic pulmonary fibrosis as well as research into Hermansky-Pudlak Syndrome.

Someone please explain to me the flaws in my logic? I’m definitely not a scientist. I’m just a patient scratching my head trying to figure this all out.

Comments

Whitey said…
sry you're having a rough itme. it does sound like it's hard out in the real world. I don't know much about the whole mouse thing either sounds pretty complicated. And good job doing your research on the whole japanese albinos. I'm praying for you. God Bless You

Popular posts from this blog

Ratner's Cheesecake

Here's another recipe from Toby! Thanks Toby......and I'll get the others posted soon! Ratner's Cheesecake and plain cookies Ratner's was a Jewish dairy restaurant in the lower East Side of Manhattan. This recipe, from my disintegrating, no longer in print Ratner's cookbook, is the closest I've ever gotten to reproducing the rich, heavy cheesecake my mother made when I was a kid. It's worth the time it takes to prepare and every last calorie. Dough Can be prepared in advance. Makes enough for two cakes. Can be frozen or used to make cookies – see recipe below. 1 cup sugar 1 teaspoon vanilla extract 1 cup shortening 1 teaspoon lemon extract 1 cup butter 2 eggs 3 cups sifted cake flour ½ teaspoon salt 2 cups all purpose flour 1 teaspoon baking powder 1. In a bowl, combine all ingredients with hands. Refrigerate 3 -4 hours, or preferably overnight. Filling (for

The next generation with Hermansky-Pudlak Syndrome

I'm so behind on posting about the trip to Puerto Rico. Since the episode of Mystery Diagnosis on Hermansky-Pudlak Syndrome ran right after we got home, it's been a little busy. These, however, are my favorite pictures from Puerto Rico. I know, not pretty senery etc - but these little guys and gals inspire me. They are the next generation of folks with HPS, and if we keep up the hard work, they will live better lives because of it. They motivate me.

Some good news about Pirfenidone

Below is a press release from Intermune, the company that makes Pirfenidone. They have essentially reviewed the various clinical trials going on, and decided that Pirfenidone is safe and well tolerated. That would pretty much go along with what we've observed in the HPS community as well. We have a few folks that have been on the drug since the late 90s and continue to do well. Of course, as a journalist, I do have to say consider the source - but at the same time, as someone in a Pirfenidone trial, it's good to know. Results of Comprehensive Safety Analysis of pirfenidone In IPF Patients Presented At European Respiratory Meeting - Analysis shows safety and tolerability of pirfenidone across four clinical trials - VIENNA, Sept. 14 /PRNewswire-FirstCall/ -- InterMune, Inc. (Nasdaq: ITMN ) today announced that the results of a comprehensive review of safety data from four clinical studies were presented at the 2009 European Respiratory Society Annual Congress in Vienna, Austria